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Dan Chung is the clinical ophthalmic lead at Spark Therapeutics.

We got an inside look at how the biotech Spark used mazes to develop a first-of-its-kind treatment for eye disease on the way to selling itself for $4...

A team of scientists came up with a new way to measure how well a treatment for a rare form of blindness worked.
Elizabeth Warren and Bernie Sanders were two of five senators who condemned Novartis's AveXis for submitting falsified data to the US FDA.

Elizabeth Warren and Bernie Sanders just slammed the Swiss drug giant Novartis over a new controversy swirling around the world’s most expensive...

"This scandal smacks of the pharmaceutical industry's privilege and greed, and Americans are sick of it," they wrote to the FDA's acting leader.
Jackson Schultheis is now eligible for the spinal muscular atrophy treatment Zolgensma after his health insurer changed its policy.

Aetna and Anthem will now pay for more kids with a devastating rare disease to get a $2.1 million drug, reversing earlier denials

Business Insider's reporting highlighted families fighting for access to the treatment, Zolgensma, which is the most expensive drug in the world.

Dispensed: A big week for digital health IPOs, what happens when a $2.1 million drug can’t get to the kids who need it, and what a top health-te...

Welcome to Dispensed, our weekly dispatch of healthcare, biotech, and pharma news from Business Insider.
Jackson Schultheis has been denied a new, $2.1 million treatment for the condition spinal muscular atrophy by health insurer Anthem Blue Cross Blue Shield.

‘Like we were being forced to gamble with our son’s life’: Health insurers won’t pay for a $2.1 million drug for kids, and par...

It's "heartbreaking," one mom said, "because this one person is everything to us. And they're acting like his life doesn't really matter."
Jonathan Lasko, 31, holds the hand of his son Max, age 3.5, who was born with spinal muscular atrophy. A new one-time treatment was just approved for the disease, with a $2.1 million price tag.

The US just approved a $2.1 million treatment for a devastating disease. It’s the most expensive drug in the world.

The treatment, called Zolgensma, should last longer than a typical drug. It also has a much higher price tag.
Iora Health CEO Rushika Fernandopulle made our list of 10 people transforming healthcare.

Dispensed: Introducing Business Insider’s 10 people transforming healthcare

Welcome to Dispensed, Business Insider's weekly newsletter giving you a dose of pharma, biotech, and healthcare news.
A new experimental gene therapy has cured babies born with a genetic disease dubbed "bubble boy" syndrome.

There’s now a cure for the deadly genetic disorder known as ‘bubble-boy’ disease

Doctors used a cutting-edge medical technique called gene therapy to treat 10 babies born with the disease. The biotech that helped saw its stock surge.
Human genetic material is stored at a laboratory in Munich.

Big pharma’s big bets, a hedge-fund rivalry, and Silicon Valley’s obsession with failing forward

Gene therapy, a decades-old technology that targets disease at its genetic root, is coming of age. New startups are pouring into the space, and it's become a hot area for M&A.

The top scientist at AveXis told us the ‘unique’ strength that powered its $9 billion sale to Novartis, and it could shape the future of g...

Manufacturing has emerged as a huge challenge for the booming gene therapy industry because these products are so new and complex.